Novel electric power-driven hydrodynamic injection system for gene delivery: safety and efficacy of human factor IX delivery in rats
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چکیده
منابع مشابه
Efficacy and Safety of Pancreas-Targeted Hydrodynamic Gene Delivery in Rats
Development of an effective, safe, and convenient method for gene delivery to the pancreas is a critical step toward gene therapy for pancreatic diseases. Therefore, we tested the possibility of applying the principle of hydrodynamic gene delivery for successful gene transfer to pancreas using rats as a model. The established procedure involves the insertion of a catheter into the superior mese...
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ژورنال
عنوان ژورنال: Gene Therapy
سال: 2013
ISSN: 0969-7128,1476-5462
DOI: 10.1038/gt.2013.2